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CADTH Canadian Drug Expert Committee Recommendation: Eliglustat (Cerdelga — Sanofi Genzyme): Indication: Type 1 Gaucher disease [Internet].
Ottawa (ON): Canadian Agency for Drugs and Technologies in Health; 2017 Jul.
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Regulatory Processes for Rare Disease Drugs in the United States and European Union: Flexibilities and Collaborative Opportunities.
National Academies of Sciences, Engineering, and Medicine; Health and Medicine Division; Board on Health Sciences Policy; Committee on Processes to Evaluate the Safety and Efficacy of Drugs for Rare Diseases or Conditions in the United States and the European Union; Shore CK, Worku TL, Smith CW, et al., editors.
Washington (DC): National Academies Press (US); 2024 Oct 30.
Developmental follow-up of children and young people born preterm.
National Guideline Alliance (UK).
London: National Institute for Health and Care Excellence (NICE); 2017 Aug. (NICE Guideline, No. 72.)
ACMG ACT Sheets and Algorithms [Internet].
Bethesda (MD): American College of Medical Genetics and Genomics; 2001-.
Updated Recommendations on Treatment of Adolescents and Children with Chronic HCV Infection, and HCV Simplified Service Delivery and Diagnostics [Internet].
Geneva: World Health Organization; 2022.
Genetic Susceptibility to Breast and Ovarian Cancer: Assessment, Counseling and Testing Guidelines.
Bethesda (MD): American College of Medical Genetics; 1999.
CADTH Reimbursement Reviews and Recommendations.
Ottawa (ON): Canadian Agency for Drugs and Technologies in Health; 2013-.
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