Etiology
Del Bufalo F,
De Angelis B,
Caruana I,
Del Baldo G,
De Ioris MA,
Serra A,
Mastronuzzi A,
Cefalo MG,
Pagliara D,
Amicucci M,
Li Pira G,
Leone G,
Bertaina V,
Sinibaldi M,
Di Cecca S,
Guercio M,
Abbaszadeh Z,
Iaffaldano L,
Gunetti M,
Iacovelli S,
Bugianesi R,
Macchia S,
Algeri M,
Merli P,
Galaverna F,
Abbas R,
Garganese MC,
Villani MF,
Colafati GS,
Bonetti F,
Rabusin M,
Perruccio K,
Folsi V,
Quintarelli C,
Locatelli F;
Precision Medicine Team–IRCCS Ospedale Pediatrico Bambino Gesù
N Engl J Med
2023 Apr 6;388(14):1284-1295.
doi: 10.1056/NEJMoa2210859.
PMID: 37018492
DuBois SG,
Macy ME,
Henderson TO
Am Soc Clin Oncol Educ Book
2022 Apr;42:1-13.
doi: 10.1200/EDBK_349783.
PMID: 35522915
Anderson J,
Majzner RG,
Sondel PM
Clin Cancer Res
2022 Aug 2;28(15):3196-3206.
doi: 10.1158/1078-0432.CCR-21-1356.
PMID: 35435953Free PMC Article
Markham A
Drugs
2021 Feb;81(2):291-296.
doi: 10.1007/s40265-021-01467-4.
PMID: 33616889
Whittle SB,
Smith V,
Doherty E,
Zhao S,
McCarty S,
Zage PE
Expert Rev Anticancer Ther
2017 Apr;17(4):369-386.
Epub 2017 Mar 15
doi: 10.1080/14737140.2017.1285230.
PMID: 28142287
Diagnosis
Costa A,
Thirant C,
Kramdi A,
Pierre-Eugène C,
Louis-Brennetot C,
Blanchard O,
Surdez D,
Gruel N,
Lapouble E,
Pierron G,
Sitbon D,
Brisse H,
Gauthier A,
Fréneaux P,
Bohec M,
Raynal V,
Baulande S,
Leclere R,
Champenois G,
Nicolas A,
Meseure D,
Bellini A,
Marabelle A,
Geoerger B,
Mechta-Grigoriou F,
Schleiermacher G,
Menger L,
Delattre O,
Janoueix-Lerosey I
J Immunother Cancer
2022 Aug;10(8)
doi: 10.1136/jitc-2022-004807.
PMID: 36054452Free PMC Article
DuBois SG,
Macy ME,
Henderson TO
Am Soc Clin Oncol Educ Book
2022 Apr;42:1-13.
doi: 10.1200/EDBK_349783.
PMID: 35522915
George SL,
Parmar V,
Lorenzi F,
Marshall LV,
Jamin Y,
Poon E,
Angelini P,
Chesler L
J Exp Clin Cancer Res
2020 May 6;39(1):78.
doi: 10.1186/s13046-020-01582-2.
PMID: 32375866Free PMC Article
Park JR,
Kreissman SG,
London WB,
Naranjo A,
Cohn SL,
Hogarty MD,
Tenney SC,
Haas-Kogan D,
Shaw PJ,
Kraveka JM,
Roberts SS,
Geiger JD,
Doski JJ,
Voss SD,
Maris JM,
Grupp SA,
Diller L
JAMA
2019 Aug 27;322(8):746-755.
doi: 10.1001/jama.2019.11642.
PMID: 31454045Free PMC Article
Whittle SB,
Smith V,
Doherty E,
Zhao S,
McCarty S,
Zage PE
Expert Rev Anticancer Ther
2017 Apr;17(4):369-386.
Epub 2017 Mar 15
doi: 10.1080/14737140.2017.1285230.
PMID: 28142287
Therapy
Del Bufalo F,
De Angelis B,
Caruana I,
Del Baldo G,
De Ioris MA,
Serra A,
Mastronuzzi A,
Cefalo MG,
Pagliara D,
Amicucci M,
Li Pira G,
Leone G,
Bertaina V,
Sinibaldi M,
Di Cecca S,
Guercio M,
Abbaszadeh Z,
Iaffaldano L,
Gunetti M,
Iacovelli S,
Bugianesi R,
Macchia S,
Algeri M,
Merli P,
Galaverna F,
Abbas R,
Garganese MC,
Villani MF,
Colafati GS,
Bonetti F,
Rabusin M,
Perruccio K,
Folsi V,
Quintarelli C,
Locatelli F;
Precision Medicine Team–IRCCS Ospedale Pediatrico Bambino Gesù
N Engl J Med
2023 Apr 6;388(14):1284-1295.
doi: 10.1056/NEJMoa2210859.
PMID: 37018492
DuBois SG,
Macy ME,
Henderson TO
Am Soc Clin Oncol Educ Book
2022 Apr;42:1-13.
doi: 10.1200/EDBK_349783.
PMID: 35522915
Anderson J,
Majzner RG,
Sondel PM
Clin Cancer Res
2022 Aug 2;28(15):3196-3206.
doi: 10.1158/1078-0432.CCR-21-1356.
PMID: 35435953Free PMC Article
Chan GC,
Chan CM
Biomolecules
2022 Feb 24;12(3)
doi: 10.3390/biom12030358.
PMID: 35327550Free PMC Article
Markham A
Drugs
2021 Feb;81(2):291-296.
doi: 10.1007/s40265-021-01467-4.
PMID: 33616889
Prognosis
DuBois SG,
Macy ME,
Henderson TO
Am Soc Clin Oncol Educ Book
2022 Apr;42:1-13.
doi: 10.1200/EDBK_349783.
PMID: 35522915
Chung C,
Boterberg T,
Lucas J,
Panoff J,
Valteau-Couanet D,
Hero B,
Bagatell R,
Hill-Kayser CE
Pediatr Blood Cancer
2021 May;68 Suppl 2(Suppl 2):e28473.
doi: 10.1002/pbc.28473.
PMID: 33818884Free PMC Article
Wienke J,
Dierselhuis MP,
Tytgat GAM,
Künkele A,
Nierkens S,
Molenaar JJ
Eur J Cancer
2021 Feb;144:123-150.
Epub 2020 Dec 18
doi: 10.1016/j.ejca.2020.11.014.
PMID: 33341446
Sait S,
Modak S
Expert Rev Anticancer Ther
2017 Oct;17(10):889-904.
Epub 2017 Aug 14
doi: 10.1080/14737140.2017.1364995.
PMID: 28780888Free PMC Article
Whittle SB,
Smith V,
Doherty E,
Zhao S,
McCarty S,
Zage PE
Expert Rev Anticancer Ther
2017 Apr;17(4):369-386.
Epub 2017 Mar 15
doi: 10.1080/14737140.2017.1285230.
PMID: 28142287
Clinical prediction guides
Del Bufalo F,
De Angelis B,
Caruana I,
Del Baldo G,
De Ioris MA,
Serra A,
Mastronuzzi A,
Cefalo MG,
Pagliara D,
Amicucci M,
Li Pira G,
Leone G,
Bertaina V,
Sinibaldi M,
Di Cecca S,
Guercio M,
Abbaszadeh Z,
Iaffaldano L,
Gunetti M,
Iacovelli S,
Bugianesi R,
Macchia S,
Algeri M,
Merli P,
Galaverna F,
Abbas R,
Garganese MC,
Villani MF,
Colafati GS,
Bonetti F,
Rabusin M,
Perruccio K,
Folsi V,
Quintarelli C,
Locatelli F;
Precision Medicine Team–IRCCS Ospedale Pediatrico Bambino Gesù
N Engl J Med
2023 Apr 6;388(14):1284-1295.
doi: 10.1056/NEJMoa2210859.
PMID: 37018492
Nijhuis A,
Sikka A,
Yogev O,
Herendi L,
Balcells C,
Ma Y,
Poon E,
Eckold C,
Valbuena GN,
Xu Y,
Liu Y,
da Costa BM,
Gruet M,
Wickremesinghe C,
Benito A,
Kramer H,
Montoya A,
Carling D,
Want EJ,
Jamin Y,
Chesler L,
Keun HC
Nat Commun
2022 Mar 16;13(1):1380.
doi: 10.1038/s41467-022-28907-3.
PMID: 35296644Free PMC Article
Anderson NM,
Qin X,
Finan JM,
Lam A,
Athoe J,
Missiaen R,
Skuli N,
Kennedy A,
Saini AS,
Tao T,
Zhu S,
Nissim I,
Look AT,
Qing G,
Simon MC,
Feng H
Cancer Res
2021 Sep 1;81(17):4417-4430.
Epub 2021 Jul 7
doi: 10.1158/0008-5472.CAN-20-2153.
PMID: 34233924Free PMC Article
Yu AL,
Gilman AL,
Ozkaynak MF,
Naranjo A,
Diccianni MB,
Gan J,
Hank JA,
Batova A,
London WB,
Tenney SC,
Smith M,
Shulkin BL,
Parisi M,
Matthay KK,
Cohn SL,
Maris JM,
Bagatell R,
Park JR,
Sondel PM
Clin Cancer Res
2021 Apr 15;27(8):2179-2189.
Epub 2021 Jan 27
doi: 10.1158/1078-0432.CCR-20-3909.
PMID: 33504555Free PMC Article
Yu AL,
Gilman AL,
Ozkaynak MF,
London WB,
Kreissman SG,
Chen HX,
Smith M,
Anderson B,
Villablanca JG,
Matthay KK,
Shimada H,
Grupp SA,
Seeger R,
Reynolds CP,
Buxton A,
Reisfeld RA,
Gillies SD,
Cohn SL,
Maris JM,
Sondel PM;
Children's Oncology Group
N Engl J Med
2010 Sep 30;363(14):1324-34.
doi: 10.1056/NEJMoa0911123.
PMID: 20879881Free PMC Article