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Paik J
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Prognosis
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CNS Drugs
2022 Sep;36(9):995-1005.
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Morton SU,
Christodoulou J,
Costain G,
Muntoni F,
Wakeling E,
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Szuto A,
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JAMA Neurol
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Hwu WL,
Crawford TO,
Finkel RS,
Kirschner J,
Kuntz NL,
Parsons JA,
Ryan MM,
Butterfield RJ,
Topaloglu H,
Ben-Omran T,
Sansone VA,
Jong YJ,
Shu F,
Staropoli JF,
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Stebbins C,
Petrillo M,
Braley G,
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NURTURE Study Group
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Parsons J,
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Chiriboga CA,
McDonald C,
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Thangarajh M,
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Finanger E,
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McGovern MM,
McNeil DE,
Finkel R,
Iannaccone ST,
Kaye E,
Kingsley A,
Renusch SR,
McGovern VL,
Wang X,
Zaworski PG,
Prior TW,
Burghes AHM,
Bartlett A,
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NeuroNEXT Clinical Trial Network on behalf of the NN101 SMA Biomarker Investigators
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D'Amico A,
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Orphanet J Rare Dis
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Clinical prediction guides
Crawford TO,
Swoboda KJ,
De Vivo DC,
Bertini E,
Hwu WL,
Finkel RS,
Kirschner J,
Kuntz NL,
Nazario AN,
Parsons JA,
Pechmann A,
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Butterfield RJ,
Topaloglu H,
Ben-Omran T,
Sansone VA,
Jong YJ,
Shu F,
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Raynaud S,
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NURTURE Study Group
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Straub V,
van Ruiten H,
Childs AM,
Ciafaloni E,
Shieh PB,
Spinty S,
Maggi L,
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Butterfield RJ,
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Manzur A,
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Ricci F,
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Kumar A,
McDonald CM,
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Joyce N,
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Gangfuss A,
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Barohn RJ,
Statland JM,
Campbell C,
Vita G,
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Hughes I,
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JAMA
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Morton SU,
Christodoulou J,
Costain G,
Muntoni F,
Wakeling E,
Wojcik MH,
French CE,
Szuto A,
Dowling JJ,
Cohn RD,
Raymond FL,
Darras BT,
Williams DA,
Lunke S,
Stark Z,
Rowitch DH,
Agrawal PB
JAMA Neurol
2022 Apr 1;79(4):405-413.
doi: 10.1001/jamaneurol.2022.0067.
PMID: 35254387Free PMC Article
Day JW,
Mendell JR,
Mercuri E,
Finkel RS,
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Kleyn A,
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Drug Saf
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Kolb SJ,
Coffey CS,
Yankey JW,
Krosschell K,
Arnold WD,
Rutkove SB,
Swoboda KJ,
Reyna SP,
Sakonju A,
Darras BT,
Shell R,
Kuntz N,
Castro D,
Parsons J,
Connolly AM,
Chiriboga CA,
McDonald C,
Burnette WB,
Werner K,
Thangarajh M,
Shieh PB,
Finanger E,
Cudkowicz ME,
McGovern MM,
McNeil DE,
Finkel R,
Iannaccone ST,
Kaye E,
Kingsley A,
Renusch SR,
McGovern VL,
Wang X,
Zaworski PG,
Prior TW,
Burghes AHM,
Bartlett A,
Kissel JT;
NeuroNEXT Clinical Trial Network on behalf of the NN101 SMA Biomarker Investigators
Ann Neurol
2017 Dec;82(6):883-891.
Epub 2017 Dec 8
doi: 10.1002/ana.25101.
PMID: 29149772Free PMC Article