Etiology
Chiesa R,
Georgiadis C,
Syed F,
Zhan H,
Etuk A,
Gkazi SA,
Preece R,
Ottaviano G,
Braybrook T,
Chu J,
Kubat A,
Adams S,
Thomas R,
Gilmour K,
O'Connor D,
Vora A,
Qasim W;
Base-Edited CAR T Group
N Engl J Med
2023 Sep 7;389(10):899-910.
Epub 2023 Jun 14
doi: 10.1056/NEJMoa2300709.
PMID: 37314354
Teachey DT,
Devidas M,
Wood BL,
Chen Z,
Hayashi RJ,
Hermiston ML,
Annett RD,
Archer JH,
Asselin BL,
August KJ,
Cho SY,
Dunsmore KP,
Fisher BT,
Freedman JL,
Galardy PJ,
Harker-Murray P,
Horton TM,
Jaju AI,
Lam A,
Messinger YH,
Miles RR,
Okada M,
Patel SI,
Schafer ES,
Schechter T,
Singh N,
Steele AC,
Sulis ML,
Vargas SL,
Winter SS,
Wood C,
Zweidler-McKay P,
Bollard CM,
Loh ML,
Hunger SP,
Raetz EA
J Clin Oncol
2022 Jul 1;40(19):2106-2118.
Epub 2022 Mar 10
doi: 10.1200/JCO.21.02678.
PMID: 35271306Free PMC Article
Brown PA,
Ji L,
Xu X,
Devidas M,
Hogan LE,
Borowitz MJ,
Raetz EA,
Zugmaier G,
Sharon E,
Bernhardt MB,
Terezakis SA,
Gore L,
Whitlock JA,
Pulsipher MA,
Hunger SP,
Loh ML
JAMA
2021 Mar 2;325(9):833-842.
doi: 10.1001/jama.2021.0669.
PMID: 33651090Free PMC Article
Pui CH
Front Med
2020 Dec;14(6):689-700.
Epub 2020 Oct 19
doi: 10.1007/s11684-020-0759-8.
PMID: 33074527Free PMC Article
Inaba H,
Mullighan CG
Haematologica
2020 Nov 1;105(11):2524-2539.
doi: 10.3324/haematol.2020.247031.
[Epub ahead of print]
PMID: 33054110Free PMC Article
Diagnosis
Teachey DT,
Devidas M,
Wood BL,
Chen Z,
Hayashi RJ,
Hermiston ML,
Annett RD,
Archer JH,
Asselin BL,
August KJ,
Cho SY,
Dunsmore KP,
Fisher BT,
Freedman JL,
Galardy PJ,
Harker-Murray P,
Horton TM,
Jaju AI,
Lam A,
Messinger YH,
Miles RR,
Okada M,
Patel SI,
Schafer ES,
Schechter T,
Singh N,
Steele AC,
Sulis ML,
Vargas SL,
Winter SS,
Wood C,
Zweidler-McKay P,
Bollard CM,
Loh ML,
Hunger SP,
Raetz EA
J Clin Oncol
2022 Jul 1;40(19):2106-2118.
Epub 2022 Mar 10
doi: 10.1200/JCO.21.02678.
PMID: 35271306Free PMC Article
Luca DC
Clin Lab Med
2021 Sep;41(3):405-416.
doi: 10.1016/j.cll.2021.04.003.
PMID: 34304772
Inaba H,
Mullighan CG
Haematologica
2020 Nov 1;105(11):2524-2539.
doi: 10.3324/haematol.2020.247031.
[Epub ahead of print]
PMID: 33054110Free PMC Article
Burkhardt B,
Hermiston ML
Br J Haematol
2019 Jun;185(6):1158-1170.
Epub 2019 Feb 27
doi: 10.1111/bjh.15793.
PMID: 30809797
Iacobucci I,
Mullighan CG
J Clin Oncol
2017 Mar 20;35(9):975-983.
Epub 2017 Feb 13
doi: 10.1200/JCO.2016.70.7836.
PMID: 28297628Free PMC Article
Therapy
Chiesa R,
Georgiadis C,
Syed F,
Zhan H,
Etuk A,
Gkazi SA,
Preece R,
Ottaviano G,
Braybrook T,
Chu J,
Kubat A,
Adams S,
Thomas R,
Gilmour K,
O'Connor D,
Vora A,
Qasim W;
Base-Edited CAR T Group
N Engl J Med
2023 Sep 7;389(10):899-910.
Epub 2023 Jun 14
doi: 10.1056/NEJMoa2300709.
PMID: 37314354
Lato MW,
Przysucha A,
Grosman S,
Zawitkowska J,
Lejman M
Int J Mol Sci
2021 Apr 26;22(9)
doi: 10.3390/ijms22094502.
PMID: 33925883Free PMC Article
Brown PA,
Ji L,
Xu X,
Devidas M,
Hogan LE,
Borowitz MJ,
Raetz EA,
Zugmaier G,
Sharon E,
Bernhardt MB,
Terezakis SA,
Gore L,
Whitlock JA,
Pulsipher MA,
Hunger SP,
Loh ML
JAMA
2021 Mar 2;325(9):833-842.
doi: 10.1001/jama.2021.0669.
PMID: 33651090Free PMC Article
Lee DW,
Santomasso BD,
Locke FL,
Ghobadi A,
Turtle CJ,
Brudno JN,
Maus MV,
Park JH,
Mead E,
Pavletic S,
Go WY,
Eldjerou L,
Gardner RA,
Frey N,
Curran KJ,
Peggs K,
Pasquini M,
DiPersio JF,
van den Brink MRM,
Komanduri KV,
Grupp SA,
Neelapu SS
Biol Blood Marrow Transplant
2019 Apr;25(4):625-638.
Epub 2018 Dec 25
doi: 10.1016/j.bbmt.2018.12.758.
PMID: 30592986
Maude SL,
Laetsch TW,
Buechner J,
Rives S,
Boyer M,
Bittencourt H,
Bader P,
Verneris MR,
Stefanski HE,
Myers GD,
Qayed M,
De Moerloose B,
Hiramatsu H,
Schlis K,
Davis KL,
Martin PL,
Nemecek ER,
Yanik GA,
Peters C,
Baruchel A,
Boissel N,
Mechinaud F,
Balduzzi A,
Krueger J,
June CH,
Levine BL,
Wood P,
Taran T,
Leung M,
Mueller KT,
Zhang Y,
Sen K,
Lebwohl D,
Pulsipher MA,
Grupp SA
N Engl J Med
2018 Feb 1;378(5):439-448.
doi: 10.1056/NEJMoa1709866.
PMID: 29385370Free PMC Article
Prognosis
van der Sluis IM,
de Lorenzo P,
Kotecha RS,
Attarbaschi A,
Escherich G,
Nysom K,
Stary J,
Ferster A,
Brethon B,
Locatelli F,
Schrappe M,
Scholte-van Houtem PE,
Valsecchi MG,
Pieters R
N Engl J Med
2023 Apr 27;388(17):1572-1581.
doi: 10.1056/NEJMoa2214171.
PMID: 37099340
Luca DC
Clin Lab Med
2021 Sep;41(3):405-416.
doi: 10.1016/j.cll.2021.04.003.
PMID: 34304772
Lato MW,
Przysucha A,
Grosman S,
Zawitkowska J,
Lejman M
Int J Mol Sci
2021 Apr 26;22(9)
doi: 10.3390/ijms22094502.
PMID: 33925883Free PMC Article
Brown PA,
Ji L,
Xu X,
Devidas M,
Hogan LE,
Borowitz MJ,
Raetz EA,
Zugmaier G,
Sharon E,
Bernhardt MB,
Terezakis SA,
Gore L,
Whitlock JA,
Pulsipher MA,
Hunger SP,
Loh ML
JAMA
2021 Mar 2;325(9):833-842.
doi: 10.1001/jama.2021.0669.
PMID: 33651090Free PMC Article
Burkhardt B,
Hermiston ML
Br J Haematol
2019 Jun;185(6):1158-1170.
Epub 2019 Feb 27
doi: 10.1111/bjh.15793.
PMID: 30809797
Clinical prediction guides
Lee SHR,
Antillon-Klussmann F,
Pei D,
Yang W,
Roberts KG,
Li Z,
Devidas M,
Yang W,
Najera C,
Lin HP,
Tan AM,
Ariffin H,
Cheng C,
Evans WE,
Hunger SP,
Jeha S,
Mullighan CG,
Loh ML,
Yeoh AEJ,
Pui CH,
Yang JJ
JAMA Oncol
2022 Mar 1;8(3):354-363.
doi: 10.1001/jamaoncol.2021.6826.
PMID: 35084434Free PMC Article
Pulsipher MA,
Han X,
Maude SL,
Laetsch TW,
Qayed M,
Rives S,
Boyer MW,
Hiramatsu H,
Yanik GA,
Driscoll T,
Myers GD,
Bader P,
Baruchel A,
Buechner J,
Stefanski HE,
Kalfoglou C,
Nguyen K,
Waldron ER,
Thudium Mueller K,
Maier HJ,
Kari G,
Grupp SA
Blood Cancer Discov
2022 Jan;3(1):66-81.
Epub 2021 Dec 1
doi: 10.1158/2643-3230.BCD-21-0095.
PMID: 35019853Free PMC Article
Hayashi RJ,
Winter SS,
Dunsmore KP,
Devidas M,
Chen Z,
Wood BL,
Hermiston ML,
Teachey DT,
Perkins SL,
Miles RR,
Raetz EA,
Loh ML,
Winick NJ,
Carroll WL,
Hunger SP,
Lim MS,
Gross TG,
Bollard CM
J Clin Oncol
2020 Sep 10;38(26):3062-3070.
Epub 2020 Jun 17
doi: 10.1200/JCO.20.00531.
PMID: 32552472Free PMC Article
Maude SL,
Laetsch TW,
Buechner J,
Rives S,
Boyer M,
Bittencourt H,
Bader P,
Verneris MR,
Stefanski HE,
Myers GD,
Qayed M,
De Moerloose B,
Hiramatsu H,
Schlis K,
Davis KL,
Martin PL,
Nemecek ER,
Yanik GA,
Peters C,
Baruchel A,
Boissel N,
Mechinaud F,
Balduzzi A,
Krueger J,
June CH,
Levine BL,
Wood P,
Taran T,
Leung M,
Mueller KT,
Zhang Y,
Sen K,
Lebwohl D,
Pulsipher MA,
Grupp SA
N Engl J Med
2018 Feb 1;378(5):439-448.
doi: 10.1056/NEJMoa1709866.
PMID: 29385370Free PMC Article
Gardner RA,
Finney O,
Annesley C,
Brakke H,
Summers C,
Leger K,
Bleakley M,
Brown C,
Mgebroff S,
Kelly-Spratt KS,
Hoglund V,
Lindgren C,
Oron AP,
Li D,
Riddell SR,
Park JR,
Jensen MC
Blood
2017 Jun 22;129(25):3322-3331.
Epub 2017 Apr 13
doi: 10.1182/blood-2017-02-769208.
PMID: 28408462Free PMC Article