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Syndrome with a Dandy-Walker malformation as major feature

MedGen UID:
798372
Concept ID:
CN202471
Disease or Syndrome
Synonym: Syndrome with a Dandy-Walker malformation as a major feature
 
Orphanet: ORPHA269546

Professional guidelines

PubMed

Klein O, Pierre-Kahn A, Boddaert N, Parisot D, Brunelle F
Childs Nerv Syst 2003 Aug;19(7-8):484-9. Epub 2003 Jul 16 doi: 10.1007/s00381-003-0782-5. PMID: 12879343

Recent clinical studies

Etiology

Alves CAPF, Sidpra J, Manteghinejad A, Sudhakar S, Massey FV, Aldinger KA, Haldipur P, Lucato LT, Ferraciolli SF, Teixeira SR, Öztekin Ö, Bhattacharya D, Taranath A, Prabhu SP, Mirsky DM, Andronikou S, Millen KJ, Barkovich AJ, Boltshauser E, Dobyns WB, Barkovich MJ, Whitehead MT, Mankad K
AJNR Am J Neuroradiol 2023 Oct;44(10):1201-1207. Epub 2023 Aug 17 doi: 10.3174/ajnr.A7967. PMID: 37591769Free PMC Article
Darouich S, Boutaud L, Bessières B, Bonnière M, Martinovic J, Mechler C, Alby C, Bernard JP, Roth P, Ville Y, Malan V, Vekemans M, Attié-Bitach T, Encha-Razavi F
Birth Defects Res 2017 Nov 15;109(19):1586-1595. Epub 2017 Jul 31 doi: 10.1002/bdr2.1093. PMID: 28758373
Forzano F, Mansour S, Ierullo A, Homfray T, Thilaganathan B
Prenat Diagn 2007 Jun;27(6):495-501. doi: 10.1002/pd.1722. PMID: 17367101
Klein O, Pierre-Kahn A, Boddaert N, Parisot D, Brunelle F
Childs Nerv Syst 2003 Aug;19(7-8):484-9. Epub 2003 Jul 16 doi: 10.1007/s00381-003-0782-5. PMID: 12879343
Osenbach RK, Menezes AH
Pediatr Neurosurg 1992;18(4):179-89. doi: 10.1159/000120660. PMID: 1472430

Diagnosis

Reis LM, Amor DJ, Haddad RA, Nowak CB, Keppler-Noreuil KM, Chisholm SA, Semina EV
Genes (Basel) 2023 Oct 17;14(10) doi: 10.3390/genes14101948. PMID: 37895297Free PMC Article
Alves CAPF, Sidpra J, Manteghinejad A, Sudhakar S, Massey FV, Aldinger KA, Haldipur P, Lucato LT, Ferraciolli SF, Teixeira SR, Öztekin Ö, Bhattacharya D, Taranath A, Prabhu SP, Mirsky DM, Andronikou S, Millen KJ, Barkovich AJ, Boltshauser E, Dobyns WB, Barkovich MJ, Whitehead MT, Mankad K
AJNR Am J Neuroradiol 2023 Oct;44(10):1201-1207. Epub 2023 Aug 17 doi: 10.3174/ajnr.A7967. PMID: 37591769Free PMC Article
Matsunaga T
Auris Nasus Larynx 2021 Apr;48(2):185-193. Epub 2020 Aug 26 doi: 10.1016/j.anl.2020.08.017. PMID: 32859446
Forzano F, Mansour S, Ierullo A, Homfray T, Thilaganathan B
Prenat Diagn 2007 Jun;27(6):495-501. doi: 10.1002/pd.1722. PMID: 17367101
Klein O, Pierre-Kahn A, Boddaert N, Parisot D, Brunelle F
Childs Nerv Syst 2003 Aug;19(7-8):484-9. Epub 2003 Jul 16 doi: 10.1007/s00381-003-0782-5. PMID: 12879343

Prognosis

Alves CAPF, Sidpra J, Manteghinejad A, Sudhakar S, Massey FV, Aldinger KA, Haldipur P, Lucato LT, Ferraciolli SF, Teixeira SR, Öztekin Ö, Bhattacharya D, Taranath A, Prabhu SP, Mirsky DM, Andronikou S, Millen KJ, Barkovich AJ, Boltshauser E, Dobyns WB, Barkovich MJ, Whitehead MT, Mankad K
AJNR Am J Neuroradiol 2023 Oct;44(10):1201-1207. Epub 2023 Aug 17 doi: 10.3174/ajnr.A7967. PMID: 37591769Free PMC Article
Darouich S, Boutaud L, Bessières B, Bonnière M, Martinovic J, Mechler C, Alby C, Bernard JP, Roth P, Ville Y, Malan V, Vekemans M, Attié-Bitach T, Encha-Razavi F
Birth Defects Res 2017 Nov 15;109(19):1586-1595. Epub 2017 Jul 31 doi: 10.1002/bdr2.1093. PMID: 28758373
Forzano F, Mansour S, Ierullo A, Homfray T, Thilaganathan B
Prenat Diagn 2007 Jun;27(6):495-501. doi: 10.1002/pd.1722. PMID: 17367101
Klein O, Pierre-Kahn A, Boddaert N, Parisot D, Brunelle F
Childs Nerv Syst 2003 Aug;19(7-8):484-9. Epub 2003 Jul 16 doi: 10.1007/s00381-003-0782-5. PMID: 12879343
Osenbach RK, Menezes AH
Pediatr Neurosurg 1992;18(4):179-89. doi: 10.1159/000120660. PMID: 1472430

Clinical prediction guides

Abdel-Salam GMH, Abdel-Hamid MS
Clin Genet 2023 Sep;104(3):356-364. Epub 2023 May 15 doi: 10.1111/cge.14357. PMID: 37190898
Darouich S, Boutaud L, Bessières B, Bonnière M, Martinovic J, Mechler C, Alby C, Bernard JP, Roth P, Ville Y, Malan V, Vekemans M, Attié-Bitach T, Encha-Razavi F
Birth Defects Res 2017 Nov 15;109(19):1586-1595. Epub 2017 Jul 31 doi: 10.1002/bdr2.1093. PMID: 28758373
Metzke-Heidemann S, Kuhling-von Kaisenberg H, Caliebe A, Janssen D, Jonat W, Grote W, von Kaisenberg CS
Am J Med Genet A 2004 Apr 15;126A(2):197-203. doi: 10.1002/ajmg.a.20563. PMID: 15057986
Klein O, Pierre-Kahn A, Boddaert N, Parisot D, Brunelle F
Childs Nerv Syst 2003 Aug;19(7-8):484-9. Epub 2003 Jul 16 doi: 10.1007/s00381-003-0782-5. PMID: 12879343

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