PubMed Clinical Queries
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Results for Clinical Studies: Therapy/Broad
5 of 226 results sorted by: Most Recent
See all results in PubMed (226)-
An exploratory open-label multicentre phase I/II trial evaluating the safety and efficacy of postnatal or prenatal and postnatal administration of allogeneic expanded fetal mesenchymal stem cells for the treatment of severe osteogenesis imperfecta in infants and fetuses: the BOOSTB4 trial protocol.
Sagar RL, et al. BMJ Open. 2024. PMID: 38834319 Free PMC article. Clinical Trial.
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Development of a Weight-Band Dosing Approach for Vosoritide in Children with Achondroplasia Using a Population Pharmacokinetic Model.
Qi Y, et al. Clin Pharmacokinet. 2024. PMID: 38649657 Free PMC article.
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Intraoperative Epiphyseal Perfusion Monitoring Does Not Reliably Predict Osteonecrosis Following Treatment of Unstable SCFE.
Ellsworth BK, et al. J Pediatr Orthop. 2024. PMID: 38411144
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Relevance of Extending FGFR3 Gene Analysis in Osteochondrodysplasia to Non-Coding Sequences: A Case Report.
Ouedraogo ZG, et al. Genes (Basel). 2024. PMID: 38397214 Free PMC article.
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Vosoritide therapy in children with achondroplasia aged 3-59 months: a multinational, randomised, double-blind, placebo-controlled, phase 2 trial.
Savarirayan R, et al. Lancet Child Adolesc Health. 2024. PMID: 37984383 Clinical Trial.