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Rare Childhood Malignant Neoplasm

MedGen UID:
821117
Concept ID:
C3828369
Neoplastic Process
Synonym: Rare Malignant Childhood Neoplasm

Definition

An infrequent malignant neoplasm that occurs during childhood. [from NCI]

Professional guidelines

PubMed

Stockklausner C, Duffert CM, Cario H, Knöfler R, Streif W, Kulozik AE; THROMKID-Plus Studiengruppe der Gesellschaft für Thrombose- und Hämostaseforschung (GTH) and of Gesellschaft für Pädiatrische Onkologie und Hämatologie (GPOH)
Ann Hematol 2021 Jul;100(7):1647-1665. Epub 2021 Mar 12 doi: 10.1007/s00277-021-04485-0. PMID: 33712866Free PMC Article
Jensterle M, Jazbinsek S, Bosnjak R, Popovic M, Zaletel LZ, Vesnaver TV, Kotnik BF, Kotnik P
Radiol Oncol 2019 Oct 25;53(4):388-396. doi: 10.2478/raon-2019-0036. PMID: 31652121Free PMC Article
Soares KC, Goldstein SD, Ghaseb MA, Kamel I, Hackam DJ, Pawlik TM
Pediatr Surg Int 2017 Jun;33(6):637-650. Epub 2017 Mar 31 doi: 10.1007/s00383-017-4083-6. PMID: 28364277

Recent clinical studies

Etiology

Lin FY, Chintagumpala MM
Clin Perinatol 2021 Mar;48(1):53-70. doi: 10.1016/j.clp.2020.12.001. PMID: 33583507
Merkel EA, Mohan LS, Shi K, Panah E, Zhang B, Gerami P
Lancet Child Adolesc Health 2019 Sep;3(9):646-654. Epub 2019 Jun 13 doi: 10.1016/S2352-4642(19)30116-6. PMID: 31204309
Rosti G, Secondino S, Necchi A, Fornarini G, Pedrazzoli P
Semin Oncol 2019 Apr;46(2):107-111. Epub 2019 Apr 24 doi: 10.1053/j.seminoncol.2019.04.001. PMID: 31076171
Terenziani M, D'Angelo P, Inserra A, Boldrini R, Bisogno G, Babbo GL, Conte M, Dall' Igna P, De Pasquale MD, Indolfi P, Piva L, Riccipetitoni G, Siracusa F, Spreafico F, Tamaro P, Cecchetto G
Pediatr Blood Cancer 2015 Jul;62(7):1202-8. Epub 2015 Jan 28 doi: 10.1002/pbc.25423. PMID: 25631333
Perilongo G, Shafford EA
Eur J Cancer 1999 Jun;35(6):953-8; discussion 958-9. doi: 10.1016/s0959-8049(99)00049-0. PMID: 10533478

Diagnosis

Rajput S, Alsubaie SA, Singh K, Huang TC, Moran SL
J Plast Reconstr Aesthet Surg 2022 Oct;75(10):3761-3767. Epub 2022 Jun 25 doi: 10.1016/j.bjps.2022.06.077. PMID: 36041974
Hmada YA, Bernieh A, Morris RW, Lewin J, Allen T
Arch Pathol Lab Med 2020 Jan;144(1):15-17. Epub 2019 Aug 7 doi: 10.5858/arpa.2019-0191-RA. PMID: 31389716
Rao R, Honavar SG
Indian J Pediatr 2017 Dec;84(12):937-944. Epub 2017 Jun 16 doi: 10.1007/s12098-017-2395-0. PMID: 28620731
Terenziani M, D'Angelo P, Inserra A, Boldrini R, Bisogno G, Babbo GL, Conte M, Dall' Igna P, De Pasquale MD, Indolfi P, Piva L, Riccipetitoni G, Siracusa F, Spreafico F, Tamaro P, Cecchetto G
Pediatr Blood Cancer 2015 Jul;62(7):1202-8. Epub 2015 Jan 28 doi: 10.1002/pbc.25423. PMID: 25631333
Saif MW
JOP 2007 Jan 9;8(1):55-63. PMID: 17228135

Therapy

Steinmeier T, Schulze Schleithoff S, Timmermann B
Clin Oncol (R Coll Radiol) 2019 Mar;31(3):142-150. Epub 2019 Jan 11 doi: 10.1016/j.clon.2018.12.005. PMID: 30639254
Fabian ID, Onadim Z, Karaa E, Duncan C, Chowdhury T, Scheimberg I, Ohnuma SI, Reddy MA, Sagoo MS
Oncogene 2018 Mar;37(12):1551-1560. Epub 2018 Jan 11 doi: 10.1038/s41388-017-0050-x. PMID: 29321667
Meyers RL, Maibach R, Hiyama E, Häberle B, Krailo M, Rangaswami A, Aronson DC, Malogolowkin MH, Perilongo G, von Schweinitz D, Ansari M, Lopez-Terrada D, Tanaka Y, Alaggio R, Leuschner I, Hishiki T, Schmid I, Watanabe K, Yoshimura K, Feng Y, Rinaldi E, Saraceno D, Derosa M, Czauderna P
Lancet Oncol 2017 Jan;18(1):122-131. Epub 2016 Nov 22 doi: 10.1016/S1470-2045(16)30598-8. PMID: 27884679Free PMC Article
Hayes-Jordan A, LaQuaglia MP, Modak S
Semin Pediatr Surg 2016 Oct;25(5):299-304. Epub 2016 Sep 14 doi: 10.1053/j.sempedsurg.2016.09.005. PMID: 27955733Free PMC Article
Müller HL
Endocr Rev 2014 Jun;35(3):513-43. Epub 2014 Jan 27 doi: 10.1210/er.2013-1115. PMID: 24467716

Prognosis

Ostrom QT, Francis SS, Barnholtz-Sloan JS
Curr Neurol Neurosci Rep 2021 Nov 24;21(12):68. doi: 10.1007/s11910-021-01152-9. PMID: 34817716Free PMC Article
Otte A, Müller HL
J Clin Endocrinol Metab 2021 Sep 27;106(10):e3820-e3836. doi: 10.1210/clinem/dgab397. PMID: 34086900
Johnston WT, Erdmann F, Newton R, Steliarova-Foucher E, Schüz J, Roman E
Cancer Epidemiol 2021 Apr;71(Pt B):101662. Epub 2020 Jan 8 doi: 10.1016/j.canep.2019.101662. PMID: 31924557
Fabian ID, Onadim Z, Karaa E, Duncan C, Chowdhury T, Scheimberg I, Ohnuma SI, Reddy MA, Sagoo MS
Oncogene 2018 Mar;37(12):1551-1560. Epub 2018 Jan 11 doi: 10.1038/s41388-017-0050-x. PMID: 29321667
Dimaras H, Kimani K, Dimba EA, Gronsdahl P, White A, Chan HS, Gallie BL
Lancet 2012 Apr 14;379(9824):1436-46. Epub 2012 Mar 12 doi: 10.1016/S0140-6736(11)61137-9. PMID: 22414599

Clinical prediction guides

Venkataramany AS, Schieffer KM, Lee K, Cottrell CE, Wang PY, Mardis ER, Cripe TP, Chandler DS
Ann Oncol 2022 Jun;33(6):578-592. Epub 2022 Mar 23 doi: 10.1016/j.annonc.2022.03.011. PMID: 35339647
Otte A, Müller HL
J Clin Endocrinol Metab 2021 Sep 27;106(10):e3820-e3836. doi: 10.1210/clinem/dgab397. PMID: 34086900
Niemeyer CM
Hematology Am Soc Hematol Educ Program 2018 Nov 30;2018(1):307-312. doi: 10.1182/asheducation-2018.1.307. PMID: 30504325Free PMC Article
Meyers RL, Maibach R, Hiyama E, Häberle B, Krailo M, Rangaswami A, Aronson DC, Malogolowkin MH, Perilongo G, von Schweinitz D, Ansari M, Lopez-Terrada D, Tanaka Y, Alaggio R, Leuschner I, Hishiki T, Schmid I, Watanabe K, Yoshimura K, Feng Y, Rinaldi E, Saraceno D, Derosa M, Czauderna P
Lancet Oncol 2017 Jan;18(1):122-131. Epub 2016 Nov 22 doi: 10.1016/S1470-2045(16)30598-8. PMID: 27884679Free PMC Article
Rosenbaum T, Wimmer K
Klin Padiatr 2014 Nov;226(6-7):309-15. Epub 2014 Jul 25 doi: 10.1055/s-0034-1382021. PMID: 25062113

Recent systematic reviews

Tyra J, Mierzwińska-Dolny P, Fishman AJ, Mierzwiński J
Int J Pediatr Otorhinolaryngol 2023 Oct;173:111699. Epub 2023 Aug 16 doi: 10.1016/j.ijporl.2023.111699. PMID: 37597314
Kumar S, Sarathi V, Lila AR, Sehemby M, Memon SS, Karlekar M, Sankhe S, Patil VA, Shah N, Bandgar T
Pituitary 2022 Dec;25(6):819-830. Epub 2022 Jul 18 doi: 10.1007/s11102-022-01250-y. PMID: 35851929
Wang Y, Reulen RC, Kremer LCM, de Vathaire F, Haupt R, Zadravec Zaletel L, Bagnasco F, Demoor-Goldschmidt C, van Dorp WJ, Haddy N, Hjorth L, Jakab Z, Kuehni CE, Lähteenmäki PM, van der Pal HJH, Sacerdote C, Skinner R, Terenziani M, Wesenberg F, Winther JF, van Leeuwen FE, Hawkins MM, Teepen JC, van Dalen EC, Ronckers CM
Eur J Cancer 2022 Apr;165:27-47. Epub 2022 Feb 21 doi: 10.1016/j.ejca.2022.01.001. PMID: 35202973
Balzer BWR, Loo C, Lewis CR, Trahair TN, Anazodo AC
J Thorac Oncol 2018 Dec;13(12):1832-1841. Epub 2018 Sep 4 doi: 10.1016/j.jtho.2018.08.2020. PMID: 30194036
Xu X, Sergi C
Contemp Clin Trials 2016 Sep;50:37-44. Epub 2016 Jul 14 doi: 10.1016/j.cct.2016.07.011. PMID: 27424218

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